Codon-Optimized RPGR Improves Stability and Efficacy of AAV8 Gene Therapy in Two Mouse Models of X-Linked Retinitis Pigmentosa

Mol Ther. 2017 May 24. pii: S1525-0016(17)30223-X. DOI:10.1016/j.ymthe.2017.05.005. [Epub ahead of print]

Fischer MD, McClements ME, Martinez-Fernandez de la Camara C, Bellingrath JS, Dauletbekov D, Ramsden SC, et al

https://www.ncbi.nlm.nih.gov/pubmed/28549772

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